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Characterization of Ribozymes Targeting a Congenital Night Blindness Mutation in Rhodopsin Mutation.
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Characterization of Ribozymes Targeting a Congenital Night Blindness Mutation in Rhodopsin Mutation.
Characterization of Ribozymes Targeting a Congenital Night Blindness Mutation in Rhodopsin Mutation. Adv Exp Med Biol. 2016; 854:509-15.
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PubMed
subject areas
Animals
Animals
Biocatalysis
Biocatalysis
Dependovirus
Dependovirus
Electroretinography
Electroretinography
Eye Diseases, Hereditary
Eye Diseases, Hereditary
Genetic Diseases, X-Linked
Genetic Diseases, X-Linked
Genetic Therapy
Genetic Therapy
Genetic Vectors
Genetic Vectors
Humans
Humans
Mice, Transgenic
Mice, Transgenic
Mutant Proteins
Mutant Proteins
Mutation
Mutation
Myopia
Myopia
Night Blindness
Night Blindness
Rhodopsin
Rhodopsin
RNA
RNA
RNA, Catalytic
RNA, Catalytic
Substrate Specificity
Substrate Specificity
Transcription, Genetic
Transcription, Genetic
authors with profiles
Shannon M Conley