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A modified ?-retrovirus vector for X-linked severe combined immunodeficiency.
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A modified ?-retrovirus vector for X-linked severe combined immunodeficiency.
A modified ?-retrovirus vector for X-linked severe combined immunodeficiency. N Engl J Med. 2014 Oct 09; 371(15):1407-17.
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PubMed
subject areas
Animals
Animals
Antigens, CD34
Antigens, CD34
DNA, Complementary
DNA, Complementary
Gammaretrovirus
Gammaretrovirus
Gene Expression
Gene Expression
Gene Silencing
Gene Silencing
Genetic Therapy
Genetic Therapy
Genetic Vectors
Genetic Vectors
Humans
Humans
Infant
Infant
Interleukin Receptor Common gamma Subunit
Interleukin Receptor Common gamma Subunit
Male
Male
Mice
Mice
Mutation
Mutation
T-Lymphocytes
T-Lymphocytes
Transduction, Genetic
Transduction, Genetic
Transgenes
Transgenes
X-Linked Combined Immunodeficiency Diseases
X-Linked Combined Immunodeficiency Diseases